FDA全球物质注册数据库(FDA Global Substance Registration System)
物质名称CASIMERSEN
异名/同义词ALL-P-AMBO-(2',3'-AZANEDIYL-P-(DIMETHYLAMINO)-P,2',3'-TRIDEOXY-2',3'-SECO)(2'-N->5')(C-A-A-T-G-C-C-A-T-C-C-T-GG-A-G-T-T-C-C-T-G) 5'-(P-(4-((2-(2-(2-HYDROXYETHOXY)ETHOXY)ETHOXY)CARBONYL)PIPERAZIN-1-YL)-N,NDIMETHYLPHOSPHONAMIDATE)
AMONDYS 45
CASIMERSEN
CASIMERSEN [INN]
CASIMERSEN [ORANGE BOOK]
CASIMERSEN [USAN]
CASIMERSEN [WHO-DD]
EXON-45: NG-12-0064
RNA, (P-DEOXY-P-(DIMETHYLAMINO)) (2',3'-DIDEOXY-2',3'-IMINO-2',3'-SECO) (2'A-5')(C-A-A-M5U-G-C-C-A-M5U-C-C-M5U-G-G-A-G-M5U-M5U-C-C-M5U-G), 5'-(P-(4-((2-(2-(2-HYDROXYETHOXY)ETHOXY)ETHOXY)CARBONYL)-1-PIPERAZINYL)-N,N-DIMETHYLPHOSPHONAMIDATE)
SRP-4045
CAS登记号1422958-19-7
物质唯一标识(Unique Ingredient Identifier)X8UHF7SX0R
分子式
国际化合物标识(International Chemical Identifier,InChI)
SMILES
分子结构式
欧洲化学品管理局注册号(ECHA)
成分类型INGREDIENT SUBSTANCE / nucleicAcid
关联数据
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