| 异名/同义词 | ADLINACOGENE CIVAPARVOVEC TRANSGENE INSERT PROMOTERLESS HUMAN COAGULATION FACTOR IX (HF9, FACTOR IX OR FIX) TRANSGENE CASSETTE, ENCODING EXONS 2-8 AND SPLICE ACCEPTOR SITE SEQUENCE (SA) FROM HF9 EXON 2, FLANKED BY A SEQUENCE HOMOLOGOUS TO THE ZINC-FINGER NUCLEASE (ZFN) CLEAVAGE SITE OF THE HUMAN ALBUMIN (HALB) INTRON 1
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