FDA全球物质注册数据库(FDA Global Substance Registration System)
物质名称ZICLUMERAN
异名/同义词CAS9 MRNA
CAS9 MRNA (MRNA000042)
MESSENGER RNA (MRNA), 5' CAPPED, ENCODING CODON-OPTIMISED CLUSTERED REGULARLY INTERSPACED SHORT PALINDROMIC REPEATS (CRISPR) ASSOCIATED PROTEIN 9 (CAS9), FLANKED BY UNTRANSLATED REGIONS (UTR) WITH SIGNIFICANT SEQUENCE HOMOLOGY TO THE XENOPUS BETA GLOBIN GENE, AND TERMINATED WITH A POLYADENYLATION (POLYA) TAIL. A KOZAK SEQUENCE PRECEDES THE OPEN READING FRAME AND THE 5' CAP IS A SYNTHETIC ANTI-REVERSE CAP ANALOGUE (ARCA); CONTAINS N1-METHYLPSEUDOURIDINE INSTEAD OF URIDINE (ALL-U>M1.PSI.)
NTLA-2001 COMPONENT MRNA000042
RNA (RECOMBINANT 5'-(M7GM-(5'->5')-PPP-G)-CAPPED ALL URIDINE->N1-METHYLPSEUDOURIDINE-SUBSTITUTED SYNTHETIC CRISPR-ASSOCIATED ENDODEOXYRIBONUCLEASE CAS9 LOW CODON A-OPTIMIZED-SPECIFYING PLUS XENOPUS LAEVIS .BETA.-GLOBIN 5'-AND 3'-UNTRANSLATED FLANKING REGION-CONTAINING POLY(A)-TAILED MESSENGER)
ZICLUMERAN [USAN]
ZICLUMERAN
ZICLUMERAN [INN]
CAS登记号2305431-29-0
物质唯一标识(Unique Ingredient Identifier)JJ5AS2HL3G
分子式
国际化合物标识(International Chemical Identifier,InChI)
SMILES
分子结构式
欧洲化学品管理局注册号(ECHA)
成分类型 / INGREDIENT SUBSTANCE
关联数据
  • 药品国际非专利名称数据库
扩展资源
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