FDA全球物质注册数据库(FDA Global Substance Registration System)
物质名称
ZILDISTROGENE VAROPARVOVEC
异名/同义词
A RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRUS TYPE 2/9 (RAAV REP2-CAP9) VECTOR, ENCODING HUMAN MICRODYSTROPHIN 5 (H-.MU.D5) UNDER CONTROL OF CK8 MUSCLE CREATINE KINASE PROMOTER AND ENHANCER ELEMENTS ZILDISTROGENE VAROPARVOVEC ZILDISTROGENE VAROPARVOVEC [INN]