FDA全球物质注册数据库(FDA Global Substance Registration System)
物质名称RETOFRAXGENE PARVEC
异名/同义词RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE RHESUS 10 (RAAVRH.10) VECTOR ENCODING THE FULL-LENGTH HUMAN FRATAXIN (FXN) PRECURSOR PROTEIN PRECEDED BY A KOZAK SEQUENCE. TRANSGENE EXPRESSION IS UNDER CONTROL OF THE SYNTHETIC CAG PROMOTER (HUMAN CYTOMEGALOVIRUS ENHANCER, CHICKEN .BETA.-ACTIN PROMOTER, RABBIT .BETA.-GLOBIN INTRON) AND TERMINATED WITH A RABBIT .BETA.-GLOBIN POLYADENYLATION SIGNAL; FLANKED BY AAV2 INVERTED TERMINAL REPEATS (ITRS)
RETOFRAXGENE PARVEC
RETOFRAXGENE PARVEC [INN]
CAS登记号3062583-58-5
物质唯一标识(Unique Ingredient Identifier)AP4CW4W3BP
分子式
国际化合物标识(International Chemical Identifier,InChI)
SMILES
分子结构式
欧洲化学品管理局注册号(ECHA)
成分类型 / INGREDIENT SUBSTANCE
关联数据
  • 药品国际非专利名称数据库
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