| 异名/同义词 | COSADOPGENE PARVEC COSADOPGENE PARVEC [INN] RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 2 (RAAV2) VECTOR ENCODING HUMAN GUANOSINE TRIPHOSPHATE CYCLOHYDROLASE I (GTP CYCLOHYDROLASE I, GTP-CH-I, GCH, GCH1) UNDER CONTROL OF A CYTOMEGALOVIRUS (CMV) IMMEDIATE-EARLY (IE) ENHANCER/PROMOTER AND A HUMAN .BETA.-GLOBIN INTRON AND TERMINATED BY A HUMAN GROWTH HORMONE POLYADENYLATION SIGNAL; FLANKED BY AAV2 INVERTED TERMINAL REPEATS (ITRS)
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