| 异名/同义词 | DNA (RECOMBINANT REPLICATION-DEFICIENT ADENO-ASSOCIATED VIRUS 9 VECTOR TN-201 SYNTHETIC CARDIAC-SELECTIVE PROMOTER PLUS HUMAN MYOSIN-BINDING PROTEIN MYBPC3 TRANSGENE PLUS SYNTHETIC POLYADENYLATION SIGNAL PLUS ADENO-ASSOCIATED VIRUS 2 INVERTED TERMINAL REPEAT FLANKS-SPECIFYING) RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 9 (RAAV9) VECTOR, ENCODING MYOSIN-BINDING PROTEIN C (MYBPC3), UNDER CONTROL OF A SYNTHETIC CARDIOMYOCYTE-SPECIFIC CARDIAC TROPONIN T2 (TNNT2) PROMOTER (PCARD1) AND A SYNTHETIC POLYADENYLATION SIGNAL; FLANKED BY ADENO-ASSOCIATED VIRUS 2 (AAV2) INVERTED TERMINAL REPEATS ZERTOMIBGENE CAZPARVOVEC ZERTOMIBGENE CAZPARVOVEC [INN]
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