DNA (RECOMBINANT REPLICATION-DEFECTIVE ADENO-ASSOCIATED VIRUS 9 VECTOR JAG201 HUMAN SYNAPSIN I GENE PROMOTER PLUS KOZAK SEQUENCE PLUS HUMAN GENE SHANK3 MINIATURE VERSION PLUS WOODCHUCK HEPATITIS VIRUS POST-TRANSCRIPTIONAL REGULATORY ELEMENT PLUS HUMAN SOMATOTROPIN GENE POLYADENYLATION SIGNAL PLUS ADENO-ASSOCIATED VIRUS 2 INVERTED TERMINAL REPEAT FLANKS-SPECIFYING) JAG201 VECTOR GENOME (WITH TRANSGENE INSERT EXPRESSION CASSETTE ENCODING MINISHANK3) TOVESANGENE PARVEC VECTOR GENOME (WITH TRANSGENE INSERT EXPRESSION CASSETTE ENCODING MINISHANK3)