FDA全球物质注册数据库(FDA Global Substance Registration System)
物质名称PERLOCLENGENE PARVEC
异名/同义词PERLOCLENGENE PARVEC
PERLOCLENGENE PARVEC [INN]
RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 9 (RAAV9) VECTOR ENCODING CODON-OPTIMISED TRIPEPTIDYL-PEPTIDASE 1 (TPP1; LYSOSOMAL PEPSTATIN-INSENSITIVE PROTEASE, CLN2 (CEROID-LIPOFUSCINOSIS NEURONAL 2)) UNDER CONTROL OF A CYTOMEGALOVIRUS (CMV) IMMEDIATE-EARLY ENHANCER/CHICKEN .BETA.-ACTIN PROMOTER WITH TRANSCRIPTION ENHANCEMENT BY THE CHICKEN .BETA.-ACTIN INTRON, TERMINATED WITH A RABBIT .BETA.-GLOBIN (RBG) POLYADENYLATION SIGNAL; FLANKED BY AAV2 INVERTED TERMINAL REPEATS (ITRS)
CAS登记号3064385-67-4
物质唯一标识(Unique Ingredient Identifier)5J5KE7G8TF
分子式
国际化合物标识(International Chemical Identifier,InChI)
SMILES
分子结构式
欧洲化学品管理局注册号(ECHA)
成分类型 / INGREDIENT SUBSTANCE
关联数据
  • 药品国际非专利名称数据库
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