FDA全球物质注册数据库(FDA Global Substance Registration System)
物质名称
NEXIGURAN
异名/同义词
SINGLE-STRANDED GUIDE RNA (SGRNA) TARGETING THE HUMAN TRANSTHYRETIN (TTR) GENE WITH ITS 5'-TERMINAL 20 NUCLEOTIDES NEXIGURAN NEXIGURAN [INN] RNA (SYNTHETIC HUMAN TRANSTHYRETIN GENE TTR-SPECIFIC SINGLE GUIDE)