| 异名/同义词 | A RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRAL VECTOR SEROTYPE 6 (AAV6) ENCODING CODON-OPTIMISED HUMAN ALPHA-GALACTOSIDASE A (GLA) UNDER CONTROL OF LIVER-SPECIFIC REGULATORY ELEMENTS (COMPRISING ENHANCER AND HEPATIC CONTROL REGION FROM THE HUMAN APOLIPOPROTEIN E (APOE) GENE, THE HUMAN .ALPHA.-1-ANTITRYPSIN (HAAT) PROMOTER, A CHIMERIC HUMAN .BETA.-GLOBIN/IGG (HBB-IGG) INTRON, AS WELL AS A WPREMUT6 REGION) AND A BOVINE GROWTH HORMONE (BGH) POLY A SEQUENCE, FLANKED BY ADENO-ASSOCIATED VIRUS 2 (AAV2) INVERTED TERMINAL REPEATS.
DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS VECTOR ST-920 LIVER-SPECIFIC ENHANCER-PROMOTER-INTRON REGULATORY MODULE PLUS HUMAN .ALPHA.-GALACTOSIDASE PRECURSOR-SPECIFYING)
ISARALGAGENE CIVAPARVOVEC
ISARALGAGENE CIVAPARVOVEC [INN]
ST920
ST-920
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