| 异名/同义词 | JAG-201
RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 9 (RAAV9) VECTOR ENCODING A MINIATURISED VERSION OF HUMAN SHANK3 (SH3 AND MULTIPLE ANKYRIN REPEAT DOMAINS 3, PROLINE-RICH SYNAPSE-ASSOCIATED PROTEIN 2 (PROSAP2); CORRESPONDING TO AMINO ACIDS 537-782, 1347-1806 OF THE FULL-LENGTH SHANK3 PROTEIN, M1>ADDED) PRECEDED BY A KOZAK SEQUENCE WITH EXPRESSION UNDER CONTROL OF THE HUMAN SYNAPSIN I PROMOTER, A WOODCHUCK HEPATITIS VIRUS POST-TRANSCRIPTIONAL REGULATORY ELEMENT (WPRE) AND A HUMAN GROWTH HORMONE (HGH) POLYADENYLATION SIGNAL; FLANKED BY AAV2 INVERTED TERMINAL REPEATS (ITRS)
TOVESANGENE PARVEC [INN]
TOVESANGENE PARVEC
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