| 异名/同义词 | DNA (RECOMBINANT REPLICATION-DEFECTIVE ADENO-ASSOCIATED VIRUS SEROTYPE 9 VECTOR UX701 MURINE TRANSTHYRETIN ENHANCER PLUS HUMAN TRANSTHYRETIN PROMOTER PLUS SIMIAN VIRUS 40 INTRON PLUS HUMAN ADENOSINE TRIPHOSPHATASE COPPER-TRANSPORTING .BETA. METAL-BINDING DOMAIN 4/5/6 TRANSGENE ATP7B-MBD456 PLUS SIMIAN VIRUS 40 POLYADENYLATION SIGNAL PLUS ADENO-ASSOCIATED VIRUS 2 INVERTED TERMINAL REPEAT FLANKS PLUS ADENO-ASSOCIATED VIRUS 2 REP REGION PLUS ADENO-ASSOCIATED VIRUS 9 CAP REGION-SPECIFYING)
RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 9 (RAAV9) VECTOR ENCODING ATPASE COPPER-TRANSPORTING BETA GENE (ATP7B, COPPER TRANSPORTING ATPASE 2), MODIFIED TO ENCODE THE LAST THREE OF THE SIX METAL-BINDING DOMAINS (ATP7B-MBD456), UNDER CONTROL OF A MURINE TRANSTHYRETIN ENHANCER/HUMAN TRANSTHYRETIN PROMOTER, WITH A SIMIAN VIRUS 40 (SV40) INTRON, TERMINATED WITH AN SV40 POLYADENYLATION SIGNAL, AND FLANKED BY ADENO-ASSOCIATED VIRUS 2 (AAV2) INVERTED TERMINAL REPEATS (ITRS)
RIVUNATPAGENE MIZIPARVOVEC
RIVUNATPAGENE MIZIPARVOVEC [INN]
RIVUNATPAGENE MIZIPARVOVEC [USAN]
UX701
UX-701
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