FDA全球物质注册数据库(FDA Global Substance Registration System)
物质名称GOLODIRSEN
异名/同义词GOLODIRSEN
GOLODIRSEN [MI]
GOLODIRSEN [ORANGE BOOK]
GOLODIRSEN [USAN]
GOLODIRSEN [WHO-DD]
NG-12-0163
RNA, (P-DEOXY-P-(DIMETHYLAMINO))(2',3'-DIDEOXY-2',3'-IMINO-2',3'-SECO)(2'A->5')(G-M5U-M5U-G-C-C-M5U-C-C-G-G-M5U-M5U-C-M5U-G-A-A-G-G-M5U-G-M5U-M5U-C), 5'-(P-(4-((2-(2-(2-HYDROXYETHOXY)ETHOXY)ETHOXY)CARBONYL)-1-PIPERAZINYL)-N,N-DIMETHYLPHOSPHONAMIDATE)
SRP-4053
VYONDYS 53
GOLODIRSEN [INN]
CAS登记号1422959-91-8
物质唯一标识(Unique Ingredient Identifier)033072U4MZ
分子式
国际化合物标识(International Chemical Identifier,InChI)
SMILES
分子结构式
欧洲化学品管理局注册号(ECHA)
成分类型INGREDIENT SUBSTANCE / nucleicAcid
关联数据
扩展资源
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